Parameter | Cohort A N = 16 | Cohort B N = 11 | Cohort C N = 7 | Total N = 34 | Group comparison | |
---|---|---|---|---|---|---|
Sex (n) | male/neut. female/neut. | 11/3 5/5 | 9/4 2/2 | 6/4 1/0 | 26/11 8/7 | p = 0.5951 |
Age [years] at onset | Mean ± SEM Range | 2.92 ± 0.33 0.75-5.62 | 3.99 ± 0.57 1.33-6.77 | 1.79 ± 0.41 0.83-3.50 | 2.93 ± 0.28 0.75-6.76 | p = 0.0182 B > C* |
Age [years] at inclusion | Mean ± SEM Range | 5.52 ± 0.63 1.02-11.18 | 6.06 ± 0.70 1.81-8.89 | 3.19 ± 0.88 0.97-6.99 | 5.21 ± 0.44 0.97-11.81 | p = 0.0522 |
Weight [Kg] | Mean ± SEM Range | 26.11 ± 3.04 7.30-26.11 | 22.15 ± 2.17 7.40-30 | 23.80 ± 6.10 10.50-58.4 | 24.36 ± 1.98 7.3-58.4 | p = 0.6262 |